Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies Avalglucosidase Alfa and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease
PHASE3
Primary Objective:
To determine the effect of avalglucosidase alfa treatme...
A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
PHASE2
This is a multi-stage, phase 2, open-label, multicenter, multinational, asc...
Status
Active Not Recruiting
Location
Regional Medical Genetics Center of New York Site Number : 8400002